Diseases Treated by Stem Cell Therapy

The medical conditions below are currently being treated with stem cell therapy. In the United States, many stem cell treatments are classified as clinical research. Several other countries are implementing treatments and also conducting clinical trials using stem cells derived from other tissue types. The list is growing every day.

For more information, please visit www.clinicaltrials.gov.

Leukemias, Lymphomas and other Blood Cancers
Acute Biphenotypic Leukemia
Acute Lymphocytic Leukemia (ALL)
Acute Myelogenous Leukemia (AML)
Acute Undifferentiated Leukemia
Adult T Cell Leukemia/Lymphoma
Chronic Lymphocytic Leukemia (CLL)
Chronic Myelogenous Leukemia (CML)
Hodgkin’s Lymphoma
Juvenile Chronic Myelogenous Leukemia (JCML)
Juvenile Myelomonocytic Leukemia (JMML)
Multiple Myeloma
Myeloid/Natural Killer Cell Precursor Leukemia
Non-Hodgkin’s Lymphoma
Prolymphocytic Leukemia
Plasma Cell Leukemia
Waldenstrom’s Macroglobulinemia

Other Cancers
Brain Tumors
Ewing Sarcoma
Neuroblastoma
Ovarian Cancer
Renal Cell Carcinoma
Rhabdomyosarcoma
Small-Cell Lung Cancer
Testicular Cancer
Thymoma (Thymic Carcinoma)

Bone Marrow Failure Disorders
Amegakaryocytosis
Aplastic Anemia (Severe)
Blackfan-Diamond Anemia
Congenital Cytopenia
Congenital Dyserythropoietic Anemia
Dyskeratosis Congenita
Fanconi Anemia
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pure Red Cell Aplasia

Hemoglobinopathies
Beta Thalassemia Major
Sickle Cell Disease

Histiocytic Disorders
Familial Erythrophagocytic Lymphohistiocytosis
Hemophagocytosis
Langerhans’ Cell Histiocytosis (Histiocytosis X)

Myelodysplastic/Myeloproliferative Disorders
Acute Myelofibrosis
Agnogenic Myeloid Metaplasia (Myelofibrosis)
Amyloidosis
Chronic Myelomonocytic Leukemia (CMML)
Essential Thrombocythemia
Polycythemia Vera
Refractory Anemias (RA) including:
-Refractory Anemia with Excess Blasts (RAEB)
-Refractory Anemia with Excess Blasts in
-Transformation (RAEB-T)
-Refractory Anemia with Ringed Sideroblasts

Inherited Metabolic Disorders
Adrenoleukodystrophy
Fucosidosis
Gaucher Disease
Hunter Syndrome (MPS-II)
Hurler Syndrome (MPS-IH)
Krabbe Disease
Lesch-Nyhan Syndrome
Mannosidosis
Maroteaux-Lamy Syndrome (MPS-VI)
Metachromatic Leukodystrophy
Mucolipidosis II (I-cell Disease)
Neuronal Ceroid Lipofuscinosis (Batten Disease)
Niemann-Pick Disease
Sandhoff Disease
Sanfilippo Syndrome (MPS-III)
Scheie Syndrome (MPS-IS)
Sly Syndrome (MPS-VII)
Tay Sachs
Wolman Disease

Inherited Immune System Disorders
Chronic Granulomatous Disease
Congenital Neutropenia
Leukocyte Adhesion Deficiency
Severe Combined Immunodeficiencies including:
-Adenosine Deaminase Deficiency
-Bare Lymphocyte Syndrome
-Chediak-Higashi Syndrome
-Kostmann Syndrome
-Omenn Syndrome
-Purine Nucleoside Phosphorylase Deficiency
-Reticular Dysgenesis
Wiskott-Aldrich Syndrome
X-Linked Lymphoproliferative Disorder

Other Inherited Disorders
Cartilage-Hair Hypoplasia
Congenital Erythropoietic Porphyria (Gunther Disease)
DiGeorge Syndrome
Osteopetrosis

Other
Chronic Active Epstein Barr
Evans Syndrome
Multiple Sclerosis
Rheumatoid Arthritis
Systemic Lupus Erythematosus
Thymic Dysplasia

Emerging Stem Cell Applications
Brain Injury
Spinal Cord Injury
Muscle & ligament regeneration
Wound Care / Burns
Cerebral Palsy
Parkinson’s Disease
Type 1 Diabetes
Heart Disease